The NPC Community is experiencing unprecedented investment and progress in developing treatments for the disease. Today, at number of companies have NPC programs underway, two of which are in later stages of regulatory review with the FDA. Additionally, there are a number of preclinical programs being funded and supported by NPC organizations, government grants, or investors. There are also a number of collaborative research programs established to tackle key aspects of the disease that are being managed by various organizations and research groups.
Accelerating the development of novel Niemann-Pick Type C therapies.
Bio, research interest, key words, contact.... should be fed from blog/DB entry.