Accelerate. Develop. Cure.

The Niemann-Pick Type C Therapy Accelerator's mission is to accelerate the development of novel Niemann-Pick Type C therapies and find a cure.

We connect families, researchers, and clinicians with information, tools, data, and funding to advance the development of Niemann-Pick Type C therapies.

The NPC Community welcomes supporters, researchers, companies, and families to get involved with the NPC community. Navigate through this website to learn more.

Neimann-Pick Type C Disease

Niemann-Pick Type C (NPC) disease is a genetic, neurodegenerative disorder which causes progressive deterioration of the nervous system. It usually affects children by interfering with their ability to metabolize cholesterol. Adult onset may also occur. Large amounts of cholesterol accumulate within the liver, spleen, and brain. This metabolic disorder leads to a series of neurological problems that are ultimately fatal…until a treatment is found.
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News and Stories

The NPC Therapy Accelerator (NTA) is working hard to forge research collaborations, connect companies to scientists, clinicians and patients, and share a common voice in communication to companies and regulators.  Listed below are areas the NTA is helping the NPC community.

Recent Announcements: On August 3rd, members of the NPC Accelerator and the NPC community hosted a 2 hour listening session with the FDA.  A detailed report of that meeting can be found below at this link:

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